FDA Approves Krystal Biotech’s VYJUVEK™: First Redosable Skin-disorder Gene Therapy
Krystal Biotech, Inc., a Pennsylvania-headquartered biotech company specialising in genetic medicines for rare diseases, announced on Friday that the US
Read more
Rare Diseases
ReCode Starts Phase 1 Trial of Inhaled Genetic Medicine for PCD
ReCode Therapeutics, announced the dosing of the first participants in a Phase 1 trial designed to evaluate the safety and
Read more
Pfizer Reports Positive Results from Phase 3 Hemophilia B Gene Therapy Study
Pfizer Inc. (NYSE: PFE) announced in late December, positive top-line results from the Phase 3 BENEGENE-2 study (NCT03861273) evaluating fidanacogene
Read more
Tezepelumab gets ODD in the US for Eosinophilic Esophagitis
Tezepelumab, developed by AstraZeneca in collaboration with Amgen, has been granted Orphan Drug Designation (ODD) in the US FDA for
Read more
Takeda and JCR to Commercialize Next-Gen Hunter Syndrome Therapy
Takeda and JCR Pharmaceuticals announced today a geo-based exclusive collaboration and license agreement to commercialize JR-141 (INN: pabinafusp alfa), an
Read more
Sanofi to buy Kadmon and its First-in-class Transplant Drug in $1.9B Deal
Sanofi announced that it will purchase U.S. biotech Kadmon to enhance its transplant business for approximately $1.9 billion. Sanofi and
Read more
Eli Lilly enters $1 billion agreement to acquire Prevail Therapeutics
Eli Lilly & Co and Prevail Therapeutics announced a definitive agreement for Lilly to acquire Prevail for a total consideration
Read more